Research News

Medical research is moving forward at a significant pace, offering hope for members of our community affected by muscular dystrophy and related neuromuscular conditions. This section will be regularly updated with the latest research news from the MDA-funded National Muscular Dystrophy Research Centre (NMDRC) and from laboratories and clinical trial centres around the globe.

Alerts of research news updates are also posted on the MDA Facebook page

If you have any questions please contact us:
Phone: +61 3 9320 9555

Duchenne MD research news update
8 May 2015
Keywords: Duchenne muscular dystrophy, idebenone, Raxone, Catena, Santhera, BioMarin, drisapersen, exon skipping, follistatin, gene therapy, clinical trial

Study finds parents frustrated with delays in MD diagnosis
28 April 2015
Keywords: Duchenne muscular dystrophy, timeline, diagnosis

New IVF technique helps family with MD
30 March 2015

Clinical trial of new steroid drug VBP15 for DMD starts
24 February 2015
Keywords: corticosteroid, prednisolone, Duchenne muscular dystrophy, VBP15, phase 1 clinical trial

Research Round-up 2014 – other muscular dystrophies and neuromuscular conditions
15 December 2014
Keywords: myotonic dystrophy, facioscapulohumeral muscular dystrophy, FSHD, limb girdle muscular dystrophy, oculopharyngeal muscular dystrophy, congenital muscular dystrophy, omigapil, myotubular myopathy, centronuclear myopathy, Emery-Dreifuss MD, myasthenia gravis, minicore myopathy, Charcot-Marie-Tooth disease, polymyositis, dermatomyositis, Ullrich CMD, Friedreich's ataxia, Bethlem myopathy, inclusion body myositis, merosin-deficient CMD, mitochondrial myopathy

Research Round-up 2014 – SMA and ALS
2 December 2014
Keywords: spinal muscular atrophy, SMA, amyotrophic lateral sclerosis, ALS, motor neurone disease, Lou Gehrig's disease, olesoxime, Trophos, Isis Pharmaceuticals, ISIS-SMNRx, clinical trial, gene therapy, Avexis, PTC Therapeutics, RG7800, riluzole, stem cells, Medicinova, MN-166, ibudilast, Tirasemtiv, diet.

Research Round-up 2014 – Duchenne and Becker muscular dystrophies
18 November 2014
Keywords: Duchenne muscular dystrophy, DMD, Becker muscular dystrophy, BMD, utrophin, clinical trial, SMT C1100, Sarepta, eteplirsen, exon skipping, drisapersen, Prosensa, sildenafil, tadalafil, PTC Therapeutics, Translarna, ataluren, follistatin, Catena, Santhera, genome surgery

Phase 3 Duchenne MD clinical trial starts recruitment
7 October 2014
Keywords: Duchenne muscular dystrophy, DMD, Sarepta, eteplirsen, exon skipping, clinical trial, Phase 3, exon 51

Clinical trial for congenital muscular dystrophy to start
22 July 2014
Keywords: Congenital muscular dystrophy, Ullrich, MDC1A, omigapil, phase 1 clinical trial, patient registry, Santhera Pharmaceuticals.

First clinical trial tackling the cause of myotonic dystrophy started
12 June 2014
Keywords: myotonic dystrophy, DM1, DM2, Isis Pharmaceuticals, ISIS-DMPKRx, phase 1 clinical trial, antisense drug.

Clinical trial of SMT C1100 for Duchenne muscular dystrophy
30 May 2014
Keywords: Summit plc, Duchenne muscular dystrophy, DMD, Becker muscular dystrophy, BMD, SMT C1100, clinical trial, utrophin

Conditional approval of ataluren for Duchenne MD recommended in Europe
27 May 2014
Keywords: ataluren, Translarna, nonsense mutation, Duchenne MD, DMD, Becker MD, BMD, clinical trial, PTC therapeutics, PTC124.

Increasing blood flow may be of benefit in Duchenne MD
13 May 2014
Keywords: Duchenne muscular dystrophy, DMD, Becker muscular dystrophy, clinical trial, PDE5 inhibitors, viagra, sildenafil, tadalafil, Cialis.

Sarepta to apply for accelerated approval of Duchenne MD drug
22 April 2014
Keywords: Duchenne muscular dystrophy, DMD, Sarepta, eteplirsen, exon skipping, clinical trial

DMD clinical trial news: drisapersen might work after all
25 March 2014
Keywords: Duchenne muscular dystrophy, exon skipping, clinical trial, Prosensa

Spinal muscular atrophy clinical trial update
17 March 2014
Keywords: Spinal muscular atrophy, SMA, clinical trial, Olesoxime, Trophos, ISIS-SMNRX, Isis Pharmaceuticals

Encouraging clinical trial results for oculopharyngeal MD
03 February 2014
Keywords: OPMD, swallowing, myoblast cell transplant

Duchenne MD clinical trial update
21 January 2014
Keywords: Sarepta Therapeutics, Prosensa , exon skipping, Duchenne muscular dystrophy, eteplirsen, drisapersen , clinical trial

New research grant to test possible MD therapy
26 November 2013
Keywords: National Muscular Dystrophy Research Centre (NMDRC), NHMRC, muscular dystrophy, treatment, ADAMTS5

Research discovers a promising alternative to steroids for muscular dystrophy
30 September 2013
Keywords: corticosteroid, prednisolone, muscular dystrophy, VBP15, mouse model

Disappointing exon skipping trial results released
25 September 2013
Keywords: GlaxoSmithKline, Prosensa, exon skipping, Duchenne muscular dystrophy, clinical trial, drisapersen

Diabetes research may help autoimmune disease
25 September 2013
Keywords: autoimmune disease myasthenia gravis, Guillain-Barre Syndrome, chronic inflammatory demyelinating polyneuropathy (CIDP), mouse model

Another clinical trial for Duchenne Muscular Dystrophy has started
09 September 2013
Keywords: Prosensa, exon skipping, clinical trial, DMD, PRO053

Duchenne exon skipping trial results published
12 August 2013
Keywords: Sarepta Therapeutics, clinical trial, eteplirsen

Burnt Sugar treatment for muscular dystrophy?
05 August 2013
Keywords: neutraceuticals, THI, mouse model



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